early-onset progressive encephalopathy-spastic ataxia-distal spinal muscular atrophy syndrome

Rare Disease

MONDO:0044651

Genes

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Clinical Trials

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Newborn Screening

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Patient Groups

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Companies Active in early-onset progressive encephalopathy-spastic ataxia-distal spinal muscular atrophy syndrome

3 approved

Organizations with approved therapies for this disease

Biogen Inc.

Other

Approved

Genentech, Inc.

Other

Approved

Novartis Gene Therapies

Other

Approved

View all companies active in early-onset progressive encephalopathy-spastic ataxia-distal spinal muscular atrophy syndrome

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early-onset progressive encephalopathy-spastic ataxia-distal spinal muscular atrophy syndrome

Patient-Friendly Information

Companies Active in early-onset progressive encephalopathy-spastic ataxia-distal spinal muscular atrophy syndrome

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