KISHO Clinical Trials

Explore the clinical trial landscape for any rare disease.

Tracking trials across 3,281 rare diseases

Search by:Disease•Gene•Symptom•Treatment•PAG•OMIM/Orphanet ID

Commonly searched:Cystic Fibrosis Duchenne Huntington's ALS Sickle Cell

Diseases with the most active trials

Ranked by the number of recruiting, active, and enrolling trials linked to each disease on ClinicalTrials.gov. Trial associations are condition-matched, not keyword-searched. Updated every 4 hours — as new trials open or close, rankings shift automatically.

cystic fibrosis

199 active trials

amyotrophic lateral sclerosis type 1

152 active trials

Duchenne muscular dystrophy

111 active trials

aortic aneurysm, familial abdominal, 1

102 active trials

cardiogenic shock

94 active trials

thrombophilia due to thrombin defect

92 active trials

familial meningioma

89 active trials

idiopathic aplastic anemia

82 active trials

acquired polycythemia vera

74 active trials

pulmonary fibrosis and/or bone marrow failure, Telomere-related, 2

73 active trials

gastrointestinal stromal tumor

68 active trials

bronchopulmonary dysplasia

65 active trials

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