spinal muscular atrophy, lower extremity-predominant, 2b, prenatal onset, autosomal dominant

Rare Disease

MONDO:0032660

Also known as:

spinal muscular atrophy, lower extremity-predominant, 2B, autosomal dominantSMALED2BSPINAL MUSCULAR ATROPHY, LOWER EXTREMITY-PREDOMINANT, 2B, PRENATAL ONSET, AUTOSOMAL DOMINANT

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Companies Active in spinal muscular atrophy, lower extremity-predominant, 2b, prenatal onset, autosomal dominant

3 approved

Organizations with approved therapies for this disease

Biogen Inc.

Other

Approved

Genentech, Inc.

Other

Approved

Novartis Gene Therapies

Other

Approved

View all companies active in spinal muscular atrophy, lower extremity-predominant, 2b, prenatal onset, autosomal dominant

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