symptomatic form of X-linked centronuclear myopathy in female carriers

Rare Disease

MONDO:0035826

Also known as:

Symptomatic form of X-linked myotubular myopathy in female carriersSymptomatic form of XLCNM in female carriersSymptomatic form of XLMTM in female carriers

Genes

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Clinical Trials

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Newborn Screening

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Patient Groups

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Companies Active in symptomatic form of X-linked centronuclear myopathy in female carriers

0 approved

Organizations with approved therapies for this disease

No approved therapies yet

Research is ongoing — 2 companies have orphan drug designations for this disease

FoldRx Pharmaceuticals, Inc., a subsidiary of Pfizer Inc.

Other

Designated

GalaGen, Inc.

Other

Designated

View all companies active in symptomatic form of X-linked centronuclear myopathy in female carriers

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