4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
15 companies found
8 approved / 26 designated
7 approved / 11 designated
4 approved / 10 designated
5 approved / 8 designated
8 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved