4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
27 companies found
70 approved / 109 designated
10 approved / 43 designated
34 designated · 0 approved
8 approved / 26 designated
9 approved / 23 designated
14 designated · 0 approved
13 designated · 0 approved
1 approved / 11 designated
4 approved / 10 designated
3 approved / 5 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved