4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
88 companies found
70 approved / 109 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
41 designated · 0 approved
14 approved / 34 designated
32 approved / 30 designated
6 approved / 29 designated
1 approved / 25 designated
23 designated · 0 approved
22 designated · 0 approved
19 designated · 0 approved
17 designated · 0 approved
16 designated · 0 approved
12 designated · 0 approved
7 approved / 11 designated
3 approved / 9 designated
8 designated · 0 approved
8 designated · 0 approved
8 designated · 0 approved
81 approved / 8 designated