4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
31 companies found
70 approved / 109 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
41 designated · 0 approved
39 designated · 0 approved
8 approved / 25 designated
1 approved / 25 designated
38 approved / 22 designated
43 approved / 14 designated
2 approved / 13 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved