4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
40 companies found
70 approved / 109 designated
47 approved / 88 designated
34 approved / 57 designated
34 designated · 0 approved
38 approved / 22 designated
17 designated · 0 approved
15 designated · 0 approved
10 approved / 9 designated
9 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved
6 approved / 6 designated
2 approved / 5 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved