4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
34 companies found
70 approved / 109 designated
34 designated · 0 approved
43 approved / 14 designated
8 designated · 0 approved
8 designated · 0 approved
2 approved / 7 designated
6 approved / 6 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
4 approved / 3 designated
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved