4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
19 companies found
29 approved / 42 designated
41 designated · 0 approved
39 designated · 0 approved
6 approved / 29 designated
1 approved / 25 designated
15 designated · 0 approved
15 designated · 0 approved
15 approved / 11 designated
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
1 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved