4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
38 companies found
8 approved / 25 designated
9 approved / 23 designated
15 designated · 0 approved
15 designated · 0 approved
11 approved / 15 designated
2 approved / 13 designated
1 approved / 10 designated
7 approved / 5 designated
1 approved / 5 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved