4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
12 companies found
26 approved / 30 designated
11 approved / 14 designated
1 approved / 9 designated
5 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
19 approved / 3 designated
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved