4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
56 companies found
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
10 approved / 43 designated
43 designated · 0 approved
29 approved / 42 designated
32 approved / 30 designated
26 approved / 30 designated
28 designated · 0 approved
22 designated · 0 approved
17 designated · 0 approved
31 approved / 16 designated
1 approved / 11 designated
10 designated · 0 approved
5 approved / 8 designated
8 designated · 0 approved
8 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved