4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
14 companies found
10 approved / 43 designated
9 approved / 24 designated
23 designated · 0 approved
1 approved / 11 designated
1 approved / 9 designated
8 designated · 0 approved
9 approved / 7 designated
6 designated · 0 approved
4 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved