4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
29 companies found
70 approved / 109 designated
8 approved / 25 designated
10 approved / 9 designated
8 designated · 0 approved
7 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved