4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
11 companies found
70 approved / 109 designated
47 approved / 88 designated
29 approved / 42 designated
39 designated · 0 approved
19 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
3 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved