4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
28 companies found
26 approved / 30 designated
8 approved / 25 designated
2 approved / 23 designated
38 approved / 22 designated
15 designated · 0 approved
4 approved / 12 designated
2 approved / 7 designated
1 approved / 5 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 3 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved