4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
22 companies found
14 approved / 34 designated
19 designated · 0 approved
16 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
3 approved / 5 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved