4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
11 companies found
70 approved / 109 designated
28 designated · 0 approved
19 approved / 23 designated
7 designated · 0 approved
1 approved / 6 designated
4 designated · 0 approved
3 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved