4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
94 companies found
70 approved / 109 designated
43 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
5 approved / 28 designated
1 approved / 25 designated
19 approved / 23 designated
19 designated · 0 approved
18 designated · 0 approved
11 approved / 15 designated
11 approved / 14 designated
1 approved / 8 designated
7 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated