4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
38 companies found
70 approved / 109 designated
23 approved / 67 designated
43 designated · 0 approved
28 designated · 0 approved
23 designated · 0 approved
19 designated · 0 approved
19 designated · 0 approved
17 designated · 0 approved
15 designated · 0 approved
26 approved / 11 designated
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
1 approved / 6 designated
2 approved / 5 designated
5 designated · 0 approved
5 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved