4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
18 companies found
47 approved / 88 designated
23 approved / 67 designated
29 approved / 42 designated
6 approved / 29 designated
1 approved / 25 designated
15 designated · 0 approved
17 approved / 13 designated
15 approved / 11 designated
10 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 approved / 1 designated
1 designated · 0 approved