4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
12 companies found
47 approved / 88 designated
1 approved / 8 designated
6 designated · 0 approved
4 approved / 4 designated
3 approved / 4 designated
2 designated · 0 approved
15 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved