4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
26 companies found
70 approved / 109 designated
38 approved / 34 designated
34 designated · 0 approved
5 approved / 28 designated
1 approved / 25 designated
43 approved / 14 designated
6 approved / 11 designated
3 approved / 11 designated
7 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
1 approved / 4 designated
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved