4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
17 companies found
41 designated · 0 approved
8 approved / 26 designated
17 approved / 13 designated
7 designated · 0 approved
6 designated · 0 approved
4 approved / 6 designated
7 approved / 5 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 approved / 3 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved