4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
10 approved / 43 designated
32 approved / 30 designated
8 designated · 0 approved
20 approved / 3 designated
3 designated · 0 approved
1 designated · 0 approved