4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
66 companies found
70 approved / 109 designated
47 approved / 88 designated
34 approved / 57 designated
39 designated · 0 approved
38 approved / 34 designated
26 approved / 30 designated
8 approved / 26 designated
2 approved / 23 designated
38 approved / 22 designated
17 designated · 0 approved
15 designated · 0 approved
43 approved / 14 designated
9 designated · 0 approved
9 designated · 0 approved
1 approved / 8 designated
7 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved