4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
13 companies found
7 designated · 0 approved
2 approved / 7 designated
6 designated · 0 approved
1 approved / 5 designated
4 designated · 0 approved
4 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved