4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
28 companies found
47 approved / 88 designated
34 approved / 57 designated
10 approved / 43 designated
39 designated · 0 approved
6 approved / 29 designated
3 approved / 20 designated
19 designated · 0 approved
3 approved / 15 designated
43 approved / 14 designated
12 designated · 0 approved
9 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved