4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
44 companies found
39 designated · 0 approved
16 designated · 0 approved
49 approved / 9 designated
9 designated · 0 approved
7 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved