4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
20 companies found
47 approved / 88 designated
23 approved / 67 designated
29 approved / 42 designated
39 designated · 0 approved
11 approved / 14 designated
9 approved / 7 designated
1 approved / 6 designated
5 designated · 0 approved
4 designated · 0 approved
8 approved / 3 designated
2 approved / 3 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
2 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved