4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
17 companies found
47 approved / 88 designated
23 approved / 67 designated
14 approved / 34 designated
6 approved / 29 designated
8 approved / 27 designated
1 approved / 6 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
2 approved / 3 designated
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
1 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved