4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
14 companies found
70 approved / 109 designated
29 approved / 42 designated
3 approved / 20 designated
17 designated · 0 approved
3 approved / 15 designated
7 designated · 0 approved
7 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
1 designated · 0 approved