4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
89 companies found
47 approved / 88 designated
43 designated · 0 approved
10 approved / 43 designated
29 approved / 42 designated
14 approved / 34 designated
32 approved / 30 designated
26 approved / 30 designated
1 approved / 25 designated
38 approved / 22 designated
15 approved / 11 designated
11 designated · 0 approved
10 designated · 0 approved
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 approved / 6 designated
5 designated · 0 approved
5 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved