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Dyskeratosis Congenita, X-Linked — Clinical Trials

MONDO:00105843 active·2 recruitingLast updated: Mar 22, 2026, 5:15 AM

Trial Landscape

Dyskeratosis Congenita, X-Linked has an emerging clinical trial program, driven by drug treatment and procedure.

Recruiting

Active Trials

By Approach

Drug Treatment3

Procedure1

Biological Therapy1

By Phase

Phase 1

Phase 2

Sponsor Types

Academic/Other3

Trial Locations

United States3 trials

Norway1 trial

Sweden1 trial

Trials often recruit across multiple countries, so totals exceed the trial count.

3 Trials

Phase 2Recruiting

NCT04232085

Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures

Sponsor:Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

United StatesStarted: Feb 2020Est. completion: Dec 2028Updated: Nov 2025

Phase 1Recruiting

NCT06817590

Nucleoside Therapy in Patients With Telomere Biology Disorders

Sponsor:Suneet Agarwal

United StatesStarted: Sep 2025Est. completion: Jun 2029Updated: Mar 2026

Phase 2Active, Not Recruiting

NCT01659606

Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita

Sponsor:Boston Children's Hospital

United StatesStarted: Jul 2012Est. completion: Dec 2034Updated: Jan 2026

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Data sourced from ClinicalTrials.gov via Kisho's automated pipeline. Trials refreshed every 4 hours for monitored diseases.

Last sync: March 22, 2026 at 5:15 AM