Phenylketonuria has an active clinical trial landscape, driven by drug treatment and gene therapy.
Recruiting
Active Trials
16 additional trials involve behavioral, dietary, diagnostic, or observational approaches.
19 trials are observational or have no phase designation.
Trials often recruit across multiple countries, so totals exceed the trial count.
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Data sourced from ClinicalTrials.gov via Kisho's automated pipeline. Trials refreshed every 4 hours for monitored diseases.
Last sync: March 16, 2026 at 10:53 AM