Orphan Drug Designations

The following drugs have received orphan drug designation from the FDA for polyarticular juvenile idiopathic arthritis. Orphan designation reflects regulatory interest and does not indicate approval for treatment.

Gene therapy approaches for polyarticular juvenile idiopathic arthritis have been reported in the published literature.

29%

Recent Publications

• Atamyıldız Uçar S (2026). [PMID: 41723586](https://pubmed.ncbi.nlm.nih.gov/41723586/). *Expert Opin Biol Ther*. [Epidemiology / Natural History]

• Ata EB (2026). [PMID: 41533222](https://pubmed.ncbi.nlm.nih.gov/41533222/). *Clin Rheumatol*. [Epidemiology / Natural History]

• Das PK (2026). [PMID: 41895033](https://pubmed.ncbi.nlm.nih.gov/41895033/). *Biologicals*. [Review / Meta-Analysis]

• Yildiz M (2026). [PMID: 41621940](https://pubmed.ncbi.nlm.nih.gov/41621940/). *J Rheumatol*. [Diagnostic / Biomarker]

• Aida Y (2026). [PMID: 42033659](https://pubmed.ncbi.nlm.nih.gov/42033659/). *Int J Rheum Dis*. [Other]

• Gundogmus F (2026). [PMID: 41780543](https://pubmed.ncbi.nlm.nih.gov/41780543/). *Klin Padiatr*. [Review / Meta-Analysis]

• Liu P (2026). [PMID: 41557167](https://pubmed.ncbi.nlm.nih.gov/41557167/). *Clin Rheumatol*. [Epidemiology / Natural History]

• Abedeen ZU (2026). [PMID: 41578476](https://pubmed.ncbi.nlm.nih.gov/41578476/). *Medicine (Baltimore)*. [Case Report / Case Series]

• Brutzkus JC (2026). [PMID: 30247840](https://pubmed.ncbi.nlm.nih.gov/30247840/). *Unknown Journal*. [Epidemiology / Natural History]

• Padda IS (2026). [PMID: 35015417](https://pubmed.ncbi.nlm.nih.gov/35015417/). *Unknown Journal*. [Epidemiology / Natural History]