A global phase III trial demonstrates the efficacy and safety of subcutaneous efgartigimod combined with prednisone in treating moderate-to-severe pemphigus. This randomized controlled study provides critical insights into potential new treatment options for this rare autoimmune disease.
efficacy and safety of subcutaneous efgartigimod with prednisone in moderate to severe pemphigus address a global phase iii randomised controlled double blind trial
Original title: “Efficacy and safety of subcutaneous efgartigimod with prednisone in moderate-to-severe pemphigus (ADDRESS): a global, phase III, randomised controlled, double-blind trial.”