A 1.5-year natural history study evaluates clinical and functional outcome measures in patients with LAMA2-related muscular dystrophy and SELENON-related myopathy. This research contributes to understanding disease progression and potential therapeutic targets.
clinical and functional outcome measures in lama2 related muscular dystrophy and selenon related myopathy a 1 5 year natural history study
Original title: “Clinical and functional outcome measures in LAMA2-related muscular dystrophy and SELENON-related myopathy; a 1.5-year natural history study.”