4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
53 companies found
70 approved / 109 designated
34 approved / 57 designated
41 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
6 approved / 29 designated
38 approved / 22 designated
3 approved / 20 designated
43 approved / 14 designated
7 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved