4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
35 companies found
29 approved / 42 designated
5 approved / 28 designated
28 designated · 0 approved
31 approved / 16 designated
16 designated · 0 approved
5 approved / 14 designated
15 approved / 11 designated
6 approved / 11 designated
3 approved / 8 designated
4 approved / 6 designated
1 approved / 5 designated
5 designated · 0 approved
5 designated · 0 approved
3 approved / 4 designated
1 approved / 4 designated
1 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved