4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
103 companies found
70 approved / 109 designated
47 approved / 88 designated
34 approved / 57 designated
43 designated · 0 approved
10 approved / 43 designated
38 approved / 34 designated
32 approved / 30 designated
28 designated · 0 approved
8 approved / 26 designated
22 designated · 0 approved
38 approved / 22 designated
3 approved / 20 designated
16 designated · 0 approved
10 designated · 0 approved
9 designated · 0 approved
8 designated · 0 approved
8 designated · 0 approved
7 designated · 0 approved
1 approved / 6 designated
1 approved / 6 designated
6 designated · 0 approved