4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
26 companies found
70 approved / 109 designated
34 approved / 57 designated
43 designated · 0 approved
29 approved / 42 designated
41 designated · 0 approved
14 approved / 34 designated
23 designated · 0 approved
19 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved
3 approved / 4 designated
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
2 approved / 1 designated