4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
24 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
28 designated · 0 approved
9 approved / 23 designated
22 designated · 0 approved
17 approved / 13 designated
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
2 approved / 6 designated
1 approved / 4 designated
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved