4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
38 companies found
10 approved / 43 designated
43 designated · 0 approved
8 approved / 27 designated
8 approved / 26 designated
18 designated · 0 approved
10 designated · 0 approved
6 designated · 0 approved
1 approved / 6 designated
6 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
27 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved