4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
58 companies found
70 approved / 109 designated
29 approved / 42 designated
38 approved / 34 designated
34 designated · 0 approved
8 approved / 27 designated
38 approved / 22 designated
31 approved / 16 designated
43 approved / 14 designated
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 approved / 6 designated
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
27 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved