4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
12 companies found
70 approved / 109 designated
32 approved / 30 designated
2 approved / 5 designated
5 designated · 0 approved
3 designated · 0 approved
3 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved