neurodegeneration with developmental delay, early respiratory failure, myoclonic seizures, and brain abnormalities

Rare Disease

MONDO:0957225

Genes

Clinical Trials

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Patient Groups

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Companies Active in neurodegeneration with developmental delay, early respiratory failure, myoclonic seizures, and brain abnormalities

1 approved

Organizations with approved therapies for this disease

UCB, Inc.

Other

Approved

View all companies active in neurodegeneration with developmental delay, early respiratory failure, myoclonic seizures, and brain abnormalities

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