4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
45 companies found
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
9 designated · 0 approved
9 designated · 0 approved
9 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved